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Sutter Children’s Center, Sacramento Administers First Spinraza Treatment in Sacramento

Posted by on Feb 23, 2017 in Children's Services, Sutter Medical Center, Sacramento | 0 comments

Charleston Goeppert, who lives with spinal muscular atrophy (SMA), loves participating in activities that well children do – like walking the family dog.

“Cash” became the first patient at Sutter Children’s Center, Sacramento to receive the groundbreaking SPINRAZA treatment on Feb. 1 in the hospital’s pediatric day unit.

Cash, as his family affectionately calls him, lives with spinal muscular atrophy (SMA), a neurological disease characterized by loss of motor neurons in the spinal cord and lower brain stem, resulting in severe and progressive muscular atrophy and weakness. Ultimately, individuals with the most severe type of SMA can become paralyzed and have difficulty performing the basic functions of life, like breathing and swallowing.

During a controlled clinical study, infantile-onset SMA patients treated with SPINRAZA achieved and sustained improvement in motor function compared to untreated study participants. In addition, a greater percentage of patients on SPINRAZA survived compared to untreated patients. In open-label studies, some patients achieved milestones such as ability to sit unassisted, stand or walk when they would otherwise be unexpected to do so and maintained milestones at ages when they would be expected to be lost.

Cash was diagnosed with SMA at 3 months old and his parents, Ashley and Cameron, have become huge advocates of SMA and treatment of the disease since his diagnosis.

SPINRAZA was FDA approved on Dec. 23, 2016, and the family moved quickly with their son’s neurologists to get his first dose administered. Sutter Children’s Center, Sacramento was the first hospital in Sacramento and third hospital in Northern California to give the treatment.

“We are so proud to be one of the first hospitals in Northern California to provide SPINRAZA to SMA patients,” said Tamara Powers, assistant administrator, women’s and children’s, Sutter Medical Center, Sacramento. “SMA is a devastating diagnosis for a family and SPINRAZA offers new hope for families and the entire SMA community.”

Cash will receive follow-up treatments of SPINRAZA for the rest of his life. The family is hopeful to see significant progress within a year of his first treatment.

Posted by on Feb 23, 2017 in Children's Services, Sutter Medical Center, Sacramento | 0 comments